Gene therapy is the use of DNA as a pharmaceutical agent to treat disease
The most common form of gene therapy involves using DNA that encodes a functional, therapeutic gene to replace a mutated gene.
Recently published: Gene Therapy Partnering Terms and Agreements
Gene therapy is the use of DNA as a pharmaceutical agent to treat disease.
It derives its name from the idea that DNA can be used to supplement or alter genes within an individual's cells as a therapy to treat disease.
The most common form of gene therapy involves using DNA that encodes a functional, therapeutic gene to replace a mutated gene.
Other forms involve directly correcting a mutation, or using DNA that encodes a therapeutic protein drug (rather than a natural human gene) to provide treatment.
In gene therapy, DNA that encodes a therapeutic protein is packaged within a "vector", which is used to get the DNA inside cells within the body.
Once inside, the DNA becomes expressed by the cell machinery, resulting in the production of therapeutic protein, which in turn treats the patient's disease.
Gene therapy partnering
Gene therapy partnering is emerging as a new trending topic for partnering in the biotech sector.
Our recent article on dealmaking summarizes the findings: Recent trends in gene therapy dealmaking
Recently published: Gene Therapy Partnering Terms and Agreements
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The Current Partnering report title: Gene Therapy Partnering Terms and Agreements
Read: more gene therapy deals in pharma, biotech, life science partnering deal news, insights and glossary
Report: Gene Therapy Partnering Terms and Agreements
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